N-Acetyl-L-Leucine improves neurological outcomes in Niemann-Pick Disease type C
1. In this randomized controlled trial, N-acetyl-L-leucine (NALL) improved neurologic status in Niemann-Pick Disease type C more effectively than a ...
Tag: Niemann-Pick disease
Improving heat-shock protein levels shows efficacy against lysosomal storage diseases [PreClinical]
1. Treatment with recombinant heat-shock protein 70 (rHSP70) reduced lysosomal enlargement in cells isolated from patients with various lysosomal storage ...
