FDA Approves First-Ever Treatment for Non-Cystic Fibrosis Bronchiectasis
Key Points: 1. First FDA-approved therapy for non-cystic fibrosis bronchiectasis; addresses a major unmet respiratory need. 2. Phase 3 data ...
Tag: cystic fibrosis
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2 Minute Medicine: Pharma Roundup – Landmark lung approval, billion-dollar obesity drug deal, oncology safety halt, and GSK’s China push [August 14 2025]
FDA Approves First-Ever Treatment for Non-Cystic Fibrosis Bronchiectasis Late last week, the U.S. Food and Drug Administration approved Insmed’s Brinsupri ...
The 2 Minute Medicine Podcast Episode 12
Welcome to the 2 Minute Medicine Podcast, summarizing the latest medical studies, curated and written by practicing physicians. On this ...
The Scan by 2 Minute Medicine®: Cystic Fibrosis and Make-A-Wish, Wyoming Bans Abortion Pills, Justin Bieber and Ramsay Hunt Syndrome, Colon Cancer in Young Adults
The Scan by 2 Minute Medicine® is a pop-culture medical newsletter and exclusive benefit for 2 Minute Medicine Plus subscribers. ...
Urine bicarbonate excretion associated with cystic fibrosis transmembrane conductance regulator function
1. In this prospective cohort study, carbonate excretion levels in cystic fibrosis (CF) patients were correlated with various disease severity ...
Newborn screening for cystic fibrosis improves nutritional outcomes
1. In this retrospective study, newborn screening for cystic fibrosis in the United States lead to improve nutritional status with higher ...
Higher body mass index associated with improved cystic fibrosis-related clinical outcomes
1. This systematic review and meta-analysis demonstrated that higher-than-normal body mass index (BMI) in patients with cystic fibrosis (CF) reduced ...
Sweat chloride levels predict future cystic fibrosis diagnosis in those with inconclusive diagnosis at birth
1. In a prospective multi-center study, 21% of children with cystic fibrosis screen positive, inconclusive diagnosis (CFSPID) at birth were ...
#VisualAbstract: Elexacaftor–Tezacaftor–Ivacaftor for Cystic Fibrosis with a Single Phe508del Allele
1. In this multicenter, phase 3 study of cystic fibrosis patients who were previously unresponsive to modulator regimens, triple-combination therapy ...
![In utero administration of ivacaftor averts multiorgan disease in ferret model of cystic fibrosis [PreClinical]](https://www.2minutemedicine.com/wp-content/uploads/2019/04/The_fluorescent_microscopy_image_of_CFTR_tagged_with_EYFP-350x250.jpg)
In utero administration of ivacaftor averts multiorgan disease in ferret model of cystic fibrosis [PreClinical]
1. A G551D missense mutation in the cystic fibrosis transmembrane conductance receptor (CFTR) is a genetic cause of cystic fibrosis ...
