Mitapivat improves clinical outcomes in patients with non-transfusion dependent thalassemia
1. Hemoglobin response was significantly greater in the treatment group compared to placebo. 2. Majority of adverse events were mild ...
Tag: mitapivat
Mitapivat may improve anemia in adults with non-transfusion dependent α- and β-thalassemia
1. 80% of patients receiving mitapivat showed hemoglobin response at 12 weeks. 2. Markers of hemolysis, such as bilirubin and ...
Mitapivat efficacious in treating pyruvate kinase deficiency
1. Compared to placebo, mitapivat was found to be effective in treating hemolytic anemia and increasing hemoglobin levels. 2. Mitapivat ...
