![In utero administration of ivacaftor averts multiorgan disease in ferret model of cystic fibrosis [PreClinical]](https://www.2minutemedicine.com/wp-content/uploads/2019/04/The_fluorescent_microscopy_image_of_CFTR_tagged_with_EYFP-350x250.jpg)
In utero administration of ivacaftor averts multiorgan disease in ferret model of cystic fibrosis [PreClinical]
1. A G551D missense mutation in the cystic fibrosis transmembrane conductance receptor (CFTR) is a genetic cause of cystic fibrosis ...
Tag: VX-770